Gene Therapy for Monogenic Disorders: Current and Pending Studies

Within the prior 24 months, I have had a financial relationship with a company producing, marketing, selling, re-selling, or distributing healthcare products used by or on patients:

• Grant Support/Research Contract - Rocket Pharma; Merck/Schering Plough; Viking; Vifor; Windtree
• Consultant Fee/Honoraria/Speaker's Bureau - Actelion; Anthem; Axon; AstraZenca; Boehringer Ingelheim; EBR Systems; Impulse Dynamics; Inventiva; Ionis; Novartis; Bristol-Myers Squibb; Astellas; Tenaya